Learn more about the gene linked to the evolutionary loss of human tails, and how, in rare cases, some people are still born ...

A Northwestern Medicine study has uncovered a promising new therapeutic approach for a rare genetic brain disorder, according ...

According to a study by an international team of researchers, summarized by the Oxford University Press, Apennine brown bears ...

Orphan Drug Designation applies to approximately 50,000 Patients who predominantly suffer from severe chronic pain due to ...

New insights into a sophisticated process that protects sperm cells has revealed a mechanism, similar to an immune system, thwarts genetic chaos during the earliest stages of their development.

Researchers are edging closer to a universal antiviral drug, a single medicine that could treat every virus known to man.

A long-established drug with a diverse medical history is drawing new attention for its potential role in treating an ultra-rare and life-threatening genetic disorder. Early findings suggest that a me ...

Across the world, only a few dozen people appear to carry a genetic glitch that lets them brush off viruses that flatten ...

Astellas Gene Therapies remains intent on treating X-linked Myotubular Myopathy (XLMTM) through a gene therapy—but instead of AAV-based resamirigene bilparvovec (AT132), Astellas is now partnering ...

Mpox may be spreading more widely in Africa than previously thought because of asymptomatic transmission, according to new ...

Rice University's SynthX Center, directed by Han Xiao, has received an up to five-year, $18 million award from the Advanced ...

An international group of researchers led by Pompeu Fabra University has discovered the nanomachine that controls ...